Overview

A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months

Status:
RECRUITING
Trial end date:
2028-06-30
Target enrollment:
Participant gender:
Summary
The purpose of this study is to evaluate the safety and efficacy of daily administration of vosoritide in participants with HCH aged 0 to \< 36 months over a 52-week period.
Phase:
PHASE2
Details
Lead Sponsor:
BioMarin Pharmaceutical
Collaborator:
ICON Clinical Research
Treatments:
vosoritide