A Study of Renal Function in Treatment-naïve, Young Male Patients With Fabry Disease
Status:
Terminated
Trial end date:
2016-09-01
Target enrollment:
Participant gender:
Summary
No investigational drug will be administered in this study for the treatment of Fabry
disease.
This will be a multicenter, multinational, non-treatment, cross-sectional study of young male
patients with Fabry disease who have not yet initiated interventional treatment for this
disease. The study will consist of a screening visit(s), a clinical investigation visit(s),
and a follow-up phone contact.
The objectives of the study are:
- To document renal function and other Fabry disease manifestations across age in
treatment-naïve, young male patients with Fabry disease.
- To provide a reference group for comparison with interventional clinical trials of Fabry
disease.
The duration of each patient's participation in the study, inclusive of the screening visit
and follow-up phone contact, will be approximately 12 weeks.