A Study Investigating the Long-term Safety and Efficacy of Deferiprone in Patients With Friedreich's Ataxia
Status:
Completed
Trial end date:
2011-03-01
Target enrollment:
Participant gender:
Summary
The primary objective of this study is to evaluate the long-term safety and tolerability of
deferiprone in subjects with Friedreich's ataxia (FRDA).
The secondary objective is to evaluate the long-term efficacy of deferiprone for the
treatment of FRDA.
The tertiary objectives are to evaluate the effect of deferiprone on:
1. cardiac function,
2. quality of life, and
3. functional status.