A Safety andTolerability Study of Multiple Doses of ISIS-DMPKRx in Adults With Myotonic Dystrophy Type 1
Status:
Completed
Trial end date:
2016-08-01
Target enrollment:
Participant gender:
Summary
This study will test the safety, tolerability, and pharmacokinetics of multiple escalating
doses of ISIS-DMPKRx administered subcutaneously to adult patients with DM1.