A Phase IIa Trial to Test Safety and Efficacy Interferon Gamma Treatment in Elevating Frataxin Levels in FRDA Patients
Status:
Completed
Trial end date:
2014-07-30
Target enrollment:
Participant gender:
Summary
The primary objective of this study is to investigate whether the treatment with IFN gamma
can induce significant accumulation of frataxin in FRDA patients, a possibility suggested by
pre-clinical evidence in an animal model of the disease.