Overview

A Phase 2a Study of TPN-101 in Patients With C9ORF72 ALS/FTD

Status:
Not yet recruiting
Trial end date:
2023-09-01
Target enrollment:
Participant gender:
Summary
This is a Phase 2a study to assess the the safety and tolerability of TPN-101 in patients with Amyotrophic Lateral Sclerosis (ALS) and/or Frontotemporal Dementia (FTD) Associated with Hexanucleotide Repeat Expansion in the C9orf72 gene (C9ORF72 ALS/FTD).
Phase:
Phase 2
Details
Lead Sponsor:
Transposon Therapeutics, Inc.