A Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
Status:
Recruiting
Trial end date:
2025-03-01
Target enrollment:
Participant gender:
Summary
This is phase 2/3 study to evaluate the safety, pharmacokinetics, pharmacodynamics, and
efficacy of the investigational product GNR-055 in MPS II (Hunter syndrome) patients of
different age groups.