Overview

A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria

Status:
Not yet recruiting
Trial end date:
2025-02-07
Target enrollment:
Participant gender:
Summary
The main purpose of this study is to evaluate the long-term safety of PTC923 in participants with phenylketonuria, and to evaluate the changes from baseline in dietary phenylalanine (Phe)/protein consumption.
Phase:
Phase 3
Details
Lead Sponsor:
PTC Therapeutics