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A B C D E F G H I J K L M N O P Q R S T U V W X Y ZClinical Trials for Genetic Diseases, X-Linked
- INcreased Sun Exposure Without Pain In Research Participants With EPP or XLP
- A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy (HOPE-3)
- A Trial of Metformin in Individuals With Fragile X Syndrome (Met)
- Smith-Lemli-Opitz Syndrome and Cholic Acid
- Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency as Open Label Extension
- A Trial of Metformin in Individuals With Fragile X Syndrome
- A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy
- Cannabidiol as an Adjunctive Treatment for Bipolar Depression
- Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy
- Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency
- An Extension Study of Ataluren (PTC124) in Participants With Nonsense Mutation Dystrophinopathy
- Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
- Immune Disorder HSCT Protocol
- Cholesterol and Antioxidant Treatment in Patients With Smith-Lemli-Opitz Syndrome (SLOS)
- SLOS: The Effect of Simvastatin in Patients Receiving Cholesterol Supplementation
- Melatonin Versus Placebo for Benzodiazepine Discontinuation in Patients With Schizophrenia
- Pharmacogenomics of Mood Stabilizer Response in Bipolar Disorder (PGBD)
- Trial of Lithium Carbonate for Treatment of Osteoporosis-pseudoglioma Syndrome
- Double-Blind Placebo-Controlled Trial of Riluzole in Pediatric Bipolar Disorder
- Interleukin-2 Treatment for Wiskott-Aldrich Syndrome
- A Preliminary Study of Sustained-Release Bupropion for Smoking Cessation in Bipolar Affective Disorder
- Cannabinoids in Bipolar Affective Disorder
- Mitochondrial Dysfunction in the Pathophysiology and Treatment of Bipolar Disorder
- Treatment of the Cholesterol Defect in Smith-Lemli-Opitz Syndrome
- Anti-Estrogens - A Potential Treatment for Bipolar Affective Disorder in Women?
- DHA and X-Linked Retinitis Pigmentosa
- Simvastatin Therapy in Smith-Lemli-Opitz Syndrome
- Allogeneic Bone Marrow Transplantation in Patients With Primary Immunodeficiencies